Kanuma®
(sebelipase alfa) intravenous infusion 20mg/10mL
Our Medicines
To date, we have six innovative medicines approved for the treatment of seven rare diseases and devastating conditions. Learn more about each of our medicines and the conditions they treat by selecting a product below.
Koselugo®
(selumetinib) 10 mg & 25 mg capsules
Soliris®
(eculizumab) injection for intravenous use 300 mg/30 mL vial
Strensiq®
(asfotase alfa) for injection 40 mg/mL
Ultomiris®
(ravulizumab-cwvz) injection for intravenous use 300 mg/3 mL vial
Voydeya™
(danicopan) 500mg-100mg tablets
Veeva ID: US/ALL/0209