Neurology
Striving to advance scientific understanding in rare neurology and to accelerate the development of potential life-changing treatments.
Innovating in Neurology
Our innovation in rare neurology spans more than a decade. By keeping patient and caregiver perspectives at the forefront, we strive to advance scientific understanding within this disease area, accelerate the development of life-changing treatments and expand access to our portfolio of medicines to patients globally, bringing new hope to the rare neurology community.
Bone Metabolism
Researching and developing innovative treatments that aim to target the underlying causes of rare bone disorders.
Cardiology
Following the science to develop and evaluate potential innovative treatment options to help people living with rare cardiology conditions.
Endocrinology
Identifying potential new opportunities to advance care for those impacted by rare endocrine diseases.
Hematology
Working to improve potential outcomes for more people living with rare hematological diseases worldwide.
Nephrology
Enhancing the understanding of rare renal diseases and accelerating
the development of potential therapies.
Rare Cancers
Striving to advance scientific understanding of rare cancers to bring
new solutions.